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Key Record Dates

ClinicalTrials.gov Identifier: NCT05163288
Brief Title: A Pivotal Study of N-Acetyl-L-Leucine on Niemann-Pick Disease Type C

First Submitted : December 6, 2021
First Submitted that Met QC Criteria : December 6, 2021
First Posted : December 20, 2021

Last Update Submitted that Met QC Criteria : September 11, 2023
Last Update Posted : September 13, 2023