Key Record Dates
ClinicalTrials.gov Identifier: | NCT05174039 |
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Brief Title: | An Open-label Safety, Pharmacokinetic, and Efficacy Study of Miglustat for the Treatment of CLN3 Disease |
First Submitted : | November 18, 2021 |
First Submitted that Met QC Criteria : | December 13, 2021 |
First Posted : | December 30, 2021 |
Last Update Submitted that Met QC Criteria : | April 25, 2024 |
Last Update Posted : | April 26, 2024 |